Developing A NextGen RNA Therapy for Rett Syndrome

So many things about Rett are beyond our control. Accelerating a cure isn’t one of them. Sign up for the Registry now to help drive the development of genetic medicines. #ParentPowered

We are the organization working to cure Rett Syndrome.

You have the power to unlock a world of information, which will entice more Biopharma companies to take on Rett.

Check your RettList today to help us bring #PharmaToTable.

So many things about Rett are beyond our control. Accelerating a cure isn’t one of them. Sign up for the Registry now to help drive the development of genetic medicines. #ParentPowered

We are the organization working to cure Rett Syndrome.

You have the power to unlock a world of information, which will entice more Biopharma companies to take on Rett.

Check your RettList today to help us bring #PharmaToTable.

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David Huss, PhD, VP, Head of Research for Shape Therapeutics discusses the company's proprietary RNA technologies and how they will be applied to fix MECP2 mutations, the root cause of Rett syndrome.

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More Resources

Our Plan for a Cure: RNA Editing

Our Plan for a Cure: RNA Trans-Splicing

$40M

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